Rare Diseases

Rare blood disorders pose a unique set of diagnostic and therapeutic challenges. Their subtle presentation can often mimic more prevalent conditions, leading to delayed diagnoses and treatment. However, recent breakthroughs in precision medicine are transforming the management of these conditions, with a focus on pioneering research in disorders like haemophilia, sickle cell disease, and transthyretin amyloidosis.

Expert video highlights and insights from the conference hub and comprehensive peer-reviewed articles from our journal portfolio provide updates on the changing treatment landscape. To learn more about how the latest developments impact on patient outcomes view our expert-led learning activities.

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